List of gene therapies
This article contains a list of commercially available gene therapies.
Gene therapies
- Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available?)
- Axicabtagene ciloleucel (Yescarta): treatment for large B-cell lymphoma
- Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia
- Brexucabtagene autoleucel (Tecartus): treatment for mantle cell lymphoma and acute lymphoblastic leukemia[1][2]
- Cambiogenplasmid (Neovasculgen): treatment for vascular endothelial growth factor peripheral artery disease
- Ciltacabtagene autoleucel (Carvykti): treatment for multiple myeloma[3]
- Elivaldogene autotemcel (Skysona): treatment for cerebral adrenoleukodystrophy
- Gendicine: treatment for head and neck squamous cell carcinoma
- Onasemnogene abeparvovec (Zolgensma): AAV-based treatment for spinal muscular atrophy
- Strimvelis: treatment for adenosine deaminase deficiency (ADA-SCID)
- Talimogene laherparepvec (Imlygic): treatment for melanoma in patients who have recurring skin lesions
- Tisagenlecleucel (Kymriah): treatment for B cell lymphoblastic leukemia
- Voretigene neparvovec (Luxturna): AAV-based treatment for Leber congenital amaurosis
See also
References
- "FDA Approves First Cell-Based Gene Therapy For Adult Patients with Relapsed or Refractory MCL". U.S. Food and Drug Administration (FDA). 24 July 2020. Retrieved 24 July 2020.
- "FDA approves brexucabtagene autoleucel for relapsed or refractory B-cell precursor acute lymphoblastic leukemia". U.S. Food and Drug Administration (FDA). 1 October 2021. Retrieved 2 October 2021.
- "FDA approves ciltacabtagene autoleucel for relapsed or refractory multiple myeloma". U.S. Food and Drug Administration (FDA). 7 March 2022. Retrieved 16 March 2022.
- Daley, Jim (1 January 2020). "Gene Therapy Arrives". Scientific American. Retrieved 9 June 2020.
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